The Medical Letter on Drugs and Therapeutics
FROM
ISSUE 1579
ISSUE 1579
August 26, 2019
Issue 1579
Subscribers: Log in to read full issue. Not a subscriber? Subscribe or purchase issue.
Note: Zolgensma Data Manipulation
August 26, 2019 (Issue: 1579)
On August 6, 2019, the FDA issued a statement on data manipulation/inaccuracy issues with Zolgensma, a virus vector-based gene therapy approved for one-time IV treatment of children <2 years old with spinal muscular atrophy.1 We reviewed Zolgensma...more
The Medical Letter is a subscriber-funded nonprofit organization that publishes critical appraisals of new prescription drugs and comparative reviews of drugs for common diseases.